EU OKs first treatment for ultra rare lysosomal storage disorder

29th August 2018 Uncategorised 0

Ultragenyx’ Mepsevii has been cleared for use in Europe to treat the ultra rare disease mucopolysaccharidosis type VII (MPS VII), offering patients an approved treatment for the very first time.

More: EU OKs first treatment for ultra rare lysosomal storage disorder
Source: News